Recently news has been released that a research group at the Scripps Research Institute in San Diago, USA have successfully cured mice with Cystinosis using stem cells from bone marrow.
This is great news and the success of the research even surprised Stephanie Cherqui, the principal investigator. There is also now discussion of clinical trials for the same treatment on humans. However, this is one step in a long road and many years of further research lie ahead. So whilst the Foundation welcomes this news, we also counsel caution in the short term.
In the meantime, we are pleased to be able to present an article summarising the research and its findings, written by Stephanie Cherqui, to whom we are very grateful.